Patient experience with hereditary and senile systemic amyloidoses: a survey from the Amyloidosis Research Consortium
نویسندگان
چکیده
Background Amyloidosis is caused by the accumulation of misfolded proteins, resulting in dysfunction of vital organs (eg, heart, kidneys, nervous system). Diagnosis and access to appropriate therapy pose significant challenges, and there is a paucity of literature depicting the patient (pt) experience. We conducted a survey to identify the challenges in establishing a diagnosis of amyloidosis and to gain insight into the pt experience.
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